Ultragenyx Pharmaceutical has dosed the first participant in Aurora, a study evaluating GTX-102 (apazunersen) for angelman ...

Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that the first patient has been dosed in the Aurora study (NCT07157254) evaluating the efficacy and safety of GTX-102 (apazunersen), an ...

Angelman syndrome is a rare disease that disrupts the normal development and function of cells, particularly in the nervous ...

For the first time, Colin Farrell has opened up his home and talked in-depth about life with his son James, who has Angelman syndrome. James was just a toddler when he was diagnosed with the rare ...

Ionis Pharmaceuticals Inc. (($IONS)) announced an update on their ongoing clinical study. Ionis Pharmaceuticals Inc. is conducting a Phase 3 study ...

HOUSTON -- Texas Children's Hospital and the Angelman Syndrome Foundation (ASF) announced the official opening of the Angelman Syndrome Clinic at Texas Children's Hospital, one of only seven Angelman ...

According to DelveInsight's estimates, the Angelman syndrome market size in the 7MM is expected to show positive growth during the forecast period (2025–2034), primarily driven by the increasing ...

Ovid Therapeutics Inc., a biopharmaceutical company, recently announced that the phase 2 STARS trial, which tested the efficacy of the investigational drug OV101, achieved its primary endpoint of ...

Henry Edberg dug through the play kitchen at his home in Rosemount before serving up the daily special to his older brother. “Vegetables are healthy, so I’m giving you the vegetables,” Henry, 3, told ...

Colin Farrel has launched a new foundation that will support adult children who have intellectual disabilities, as he opened up about his son James Farrell for the first time. The Banshees of ...

Colin Farrell revealed that his 20-year-old son, James, has been living with a disorder known as Angelman Syndrome. While speaking with PEOPLE in a recent interview, the Saving Mr. Banks star, 48, ...

New York, Aug. 26, 2020 (GLOBE NEWSWIRE) -- Reportlinker.com announces the release of the report "Angelman Syndrome Market Insights, Epidemiology, and Market Forecast ...